Discover and read the best of Twitter Threads about #hemophiliaA
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@CroteauMD up next on multiyear follow-up on SPK-8011 - an AAV vector factor 8 product. Note that the doses have been much lower than other doses investigated. Must know this as you compare these gene therapies in #hemophiliaA #ASH22 1/n 
@CroteauMD Tiny font but she is pointing out the stable lines for the activity over the years (5 years of data) -- but also to my eye the variability based on same vector doses depending on the patient. #ASH22 2/n
@CroteauMD And you don't need to zoom on these graphs -- lots of bars on the left, no bars on the right (post infusion) for need for FVIII infusion! #ASH22 3/n
